Novazyme Pharmaceuticals, Inc. has received formal notification from the Office of Orphan Products Development at the FDA that its proprietary, highly phosphorylated enzyme replacement therapy for the treatment of Pompe Disease has been granted orphan drug status. This notification from the FDA represents the first official validation of Novazyme‘s core phosphorylation technology platform with which Read more about Pompe Disease Therapy Receives Orphan Designation[…]